학술논문
Real-world evidence in achondroplasia: considerations for a standardized data set
Document Type
Article
Author
Alanay, Y.; Mohnike, K.; Nilsson, O.; Alves, I.; AlSayed, M.; Appelman-Dijkstra, N.M.; Baujat, G.; Cormier-Daire, V.; Ben-Omran, T.; Breyer, S.; Gregersen, P.A.; Guillén-Navarro, E.; Högler, W.; Maghnie, M.; Mukherjee, S.; Cohen, S.; Pimenta, J.; Sabir, I.; Selicorni, A.; Semler, J.O.; Sigaudy, S.; Popkov, D.; Noval, S.; Sessa, M.; Irving, M.
Source
In: Orphanet Journal of Rare Diseases . (Orphanet Journal of Rare Diseases, December 2023, 18(1))
Subject
Language
English
ISSN
17501172