학술논문
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Academic Journal
Value in health : the journal of the International Society for Pharmacoeconomics and Outcomes Research. 24(10):1490-1498
Academic Journal
Lingineni, Karthik; Aggarwal, Varun; Morales, Juan Francisco; Conrado, Daniela J.; Corey, Diane; Vong, Camille; Burton, Jackson; Larkindale, Jane; Romero, Klaus; Schmidt, Stephan; Kim, Sarah; Mcdonald, C; Henricson, E; Cregan, M; Johnson, L; Han, J; Joyce, N; Nicorici, A; Reddy, D; Mah, J; Chiu, A; Haig, T; Harris, M; Kornelsen, M; Rincon, N; Sanchez, K; Walker, L; Tulinius, M; Alhander, A; Ekstrom, A; Gustafsson, A; Kroksmark, A; Sterky, U; Wahlgren, L; Leshner, R; Brody, N; Drogo, B; Leach, M; Tesi‐Rocha, C; Birkmeier, M; Tadese, B; Toles, A; Thangarajh, M; Kornberg, A; Carroll, K; Devalle, K; Kennedy, R; Rodriguez, V; Villano, D; Nevo, Y; Adani, R; Barleve, A; Chen‐Joseph, L; Daana, M; Panteleyev‐Yitshak, V; Simchovitz, E; Yaffe, D; Andreone, L; Bonaudo, F; Corderi, J; Levi, L; Mesa, L; Marco, P; Clemens, P; Abdel‐Hamid, H; Bendixen, R; Bise, C; Craig, A; Karnavas, K; Matthews, C; Niizawa, G; Smith, A; Weimer, J; Anger, J; Christenson, T; Florence, J; Gadeken, R; Golumbak, P; Malkus, B; Pestronk, A; Renna, R; Schierbecker, J; Seiner, C; Wulf, C; Teasley, J; Blair, S; Grillo, B; Monasterio, E; Bertorini, T; Barrett‐Adair, M; Benzel, C; Carter, K; Clift, J; Gatlin, B; Henegar, R; Holloway, J; Igarashi, M; Kiphut, F; Parker, A; Phillips, A; Young, R; North, K; Cornett, K; Gabriel, N; Harman, M; Miller, C; Rose, K; Wicks, S; Kolski, H; Chen, L; Kennedy, C; Beneggi, M; Capone, L; Molteni, A; Morettini, V; Lotze, T; Gupta, A; Knight, A; Lott, B; Mcneil, R; Orozco, G; Schlosser, R; Chambers, G; Day, J; Dalton, J; Erickson, A; Margolis, M; Marsh, J; Naughton, C; Coleman‐Wood, K; Hoffman, A; Korn‐Petersen, W; Kuntz, N; Deliz, B; Espada, S; Fuste, P; Luciano, C; Torres, J; Morgenroth, Lauren; Ahmed, M; Arrieta, A; Bartley, N; Brown‐Caines, T; Carty, C; Duong, T; Feng, J; Hu, F; Hunegs, L; Sund, Z; Tang, W; Zimmerman, A; Nuckolls, Glen; Carifi, Emily
CPT: Pharmacometrics & Systems Pharmacology. March 2022, Vol. 11 Issue 3, p318, 15 p.
Academic Journal
In Value in Health January 2022 25(1) Supplement:S218-S218
Academic Journal
Bushby, K; Finkel, R; Wong, B; Barohn, R; Campbell, C; Comi, GP; Connolly, AM; Day, JW; Flanigan, KM; Goemans, N; Jones, KJ; Mercuri, E; Quinlivan, R; Renfroe, JB; Russman, B; Ryan, MM; Tulinius, M; Voit, T; Moore, SA; Sweeney, HL; Abresch, RT; Coleman, KL; Eagle, M; Florence, J; Gappmaier, E; Glanzman, AM; Henricson, E; Barth, J; Elfring, GL; Reha, A; Spiegel, RJ; O'Donnell, MW; Peltz, SW; McDonald, CM
Muscle & nerve. 50(4):477-487
Academic Journal
Conrado, DJ; Larkindale, J; Berg, A; Hill, M; Burton, J; Abrams, KR; Abresch, RT; Bronson, A; Chapman, D; Crowther, M; Duong, T; Gordish-Dressman, H; Harnisch, L; Henricson, E; Kim, S; McDonald, CM; Schmidt, S; Vong, C; Wang, XX; Wong, BL; Yong, F; Romero, K
Journal of pharmacokinetics and pharmacodynamics. 46(5):441-455
Academic Journal
Klingels, K; Mayhew, A G; Mazzone, E S; Duong, T; Decostre, V; Werlauff, U; Vroom, E; Mercuri, E; Goemans, N M; Eagle, M; De Groot, I; Main, M; Messina, S; Campion, G; Servais, L; Van den Hauwe, M; Es, E; Pane, M; Buccella, F; Kuijer, J; Ceradini, F; Henricson, E; McDonald, C; Florence, J
Developmental Medicine & Child Neurology. Feb 01, 2017 59(2):224-231
Academic Journal
Escolar, DM; Buyse, G; Henricson, E; Leshner, R; Florence, J; Mayhew, J; Tesi-Rocha, C; Gorni, K; Pasquali, L; Patel, KM; McCarter, R; Huang, J; Mayhew, T; Bertorini, T; Carlo, J; Connolly, AM; Clemens, PR; Goemans, N; Iannaccone, ST; Igarashi, M; Nevo, Y; Pestronk, A; Subramony, SH; Vedanarayanan, VV; Wessel, H; CINRG Grp
Conference
Buyse, G; Voit, T; McDonald, C; Gordish-Dressman, H; Henricson, E; Serjesen, T; Bernert, G; D'Angelo, M; Leinonen, M
NEUROMUSCULAR DISORDERS. 30:S130-S130
Academic Journal
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