학술논문
AAV5-MIHTT GENE THERAPY DEMONSTRATES BROAD DISTRIBUTION AND STRONG HUMAN MUTANT HUNTINGTIN LOWERING IN A HUNTINGTON DISEASE MINIPIG MODEL
Document Type
Journal
Author
Klima, Jiri; Evers, Melvin M.; Miniarikova, Jana; Juhas, Stefan; Valles, Astrid; Bohuslavova, Bozena; Juhasova, Jana; Skalnikova, Helena Kupcova; Vodicka, Petr; Valekova, Ivona; Brouwers, Cynthia; Blits, Bas; Lubelski, Jacek; Kovarova, Hana; van Deventer, Sander J.; Petry, Harald; Motlik, Jan; Konstantinova, Pavlina; Ellederova, Zdenka
Source
Subject
Language
English
ISSN
1468330X