학술논문
Relationship between Endogenous, Transgene FVIII Expression and Bleeding Events Following Valoctocogene Roxaparvovec Gene Transfer for Severe Hemophilia A: A Post-Hoc Analysis of the GENEr8-1 Phase 3 Trial
Document Type
Abstract
Author
Pipe, Steven W; Ozelo, Margareth C; Kenet, Gili; Reding, Mark T; Mason, Jane; Leavitt, Andrew D; Madan, Bella; Laffan, Michael; Quon, Doris V.; von Drygalski, Annette; Chou, Sheng-Chieh; Shapiro, Susan; Dunn, Amy L; Wang, Michael; Key, Nigel S; Kaczmarek, Radoslaw; Symington, Emily; Lawal, Adebayo; Mahajan, Reena; Chavele, Konstantia-Maria; Reddy, Divya B; Yu, Hua; Wong, Wing Yen; Robinson, Tara M; Kim, Benjamin
Source
In Blood 23 November 2021 138 Supplement 1:3972-3972
Subject
Language
ISSN
0006-4971