학술논문
Antisense oligonucleotide targeting DMPK in patients with myotonic dystrophy type 1: a multicentre, randomised, dose-escalation, placebo-controlled, phase 1/2a trial
Document Type
Article
Author
Thornton, Charles A; Moxley, Richard Thomas, III; Eichinger, Katy; Heatwole, Chad; Mignon, Laurence; Arnold, W David; Ashizawa, Tetsuo; Day, John W; Dent, Gersham; Tanner, Matthew K; Duong, Tina; Greene, Ericka P; Herbelin, Laura; Johnson, Nicholas E; King, Wendy; Kissel, John T; Leung, Doris G; Lott, Donovan J; Norris, Daniel A; Pucillo, Evan M; Schell, Wendy; Statland, Jeffrey M; Stinson, Nikia; Subramony, Sub H; Xia, Shuting; Bishop, Kathie M; Bennett, C Frank
Source
In The Lancet Neurology March 2023 22(3):218-228
Subject
Language
ISSN
1474-4422